Most are designed to target rare genetic diseases, including haemophilia B, where mutation causes problems with blood clotting.

大多数药物旨在针对罕见的遗传，包括 B 型血友，这种的突变会导致凝血问题。

To prevent complications from an existing blood or bleeding disorder, such as sickle cell disease, thalassemia, or anaemia caused by kidney disease, haemophilia, or von Willebrand disease.

预有血液出血的并发症，如镰状细胞、地中海贫血由肾脏、血友血管血友引起的贫血。

And I guess I started modifying my behaviour somewhat because the haemophilia treatment centre I was calling in to to get my medication, you'd get various brands of it and I was frankly nervous of American brands.

我想我开始稍微改变我的行为是因为我打电话到血友治疗中心拿药，你会得到各种品牌的药物， 坦率地说，我对美国品牌感到紧张。