3.Dyskeratosis congenita (DKC) is a rare inherited disease characterized by the triad of abnormal skin pigmentation, nail dystrophy, and mucosal leukoplakia.
10.Editing the unhealthy cells of those suffering from genetic diseases such as Duchenne's muscular dystrophy and cystic fibrosis will alleviate their suffering.
16.This means genetic diseases such as haemophilia, muscular dystrophy and cancers, in principle, might be " corrected" by editing the DNA of human embryos.
18.Now, the fact that both Duchenne and Becker muscular dystrophy result from mutations in the same dystrophin gene means that they are " allelic disorders, "
19.And then you would be one of hundreds of millions of people with a genetic disease, such as sickle cell anemia or progeria or muscular dystrophy or Tay-Sachs disease.
20.In addition to those two, genetic mutations in other genes are responsible for several dozen other muscular dystrophies, some of which code for proteins that form a protein complex with dystrophin protein.